Journal

Molecular Therapy

ISSN 1525-0016 · Elsevier BV

Published here

10 counted works of 10 linked

YearTitleAcademicsSources
2026 Restoration of the immune system with base editing and non-genotoxic conditioning in a Rag2 point-mutant mouse model David R. Liu CV
2025 Systematic Empirical Evaluation of Individual Base Editing Targets: Validating Therapeutic Targets in USH2A and Comparison of Methods David R. Liu CV
2024 Adenovirus Capsid-Based Anti-Fentanyl Vaccine Protects Against Fentanyl-Induced Cardio-Respiratory Depression Tristan Lambert GS
2024 Introducing a Hemoglobin G-Makassar Variant in HSCs by In Vivo Base Editing Treats Sickle Cell Disease in Mice David R. Liu CV
2023 Rescue of Hearing by Adenine Base Editing in a Humanized Mouse Model of Usher Syndrome Type 1F David R. Liu CV
2022 Adenovirus Capsid Proteins-Based Anti-Fentanyl Vaccine Attenuates Fentanyl-Induced Behaviors in Mice Tristan Lambert GS
2022 Disruption of HIV-1 Co-Receptors CCR5 and CXCR4 in Primary Human T Cells and Hematopoietic Stem and Progenitor Cells Using Base Editing David R. Liu CV
2021 Development of an Effective Anti-Fentanyl Vaccine Based on the Highly Immunogenic Adenovirus Capsid Proteins Tristan Lambert GS
2021 In Vivo Somatic Cell Base Editing and Prime Editing David R. Liu CV
2011 LiGluR Restores Visual Responses in Rodent Models of Inherited Blindness Dirk Trauner CV OA GS